I heard from a gene therapy scientist that FDA was barred by HHS from participating on Thursday in FDA's own joint workshop w/ ASGCT—the FDA/ASGCT joint workshop on AAV gene therapies. Attendees weren't able to get regulatory input from FDA during the 2nd day of the meeting as planned #biosky
January 24, 2025 at 7:16 PM
I heard from a gene therapy scientist that FDA was barred by HHS from participating on Thursday in FDA's own joint workshop w/ ASGCT—the FDA/ASGCT joint workshop on AAV gene therapies. Attendees weren't able to get regulatory input from FDA during the 2nd day of the meeting as planned #biosky
💡 Congratulations to our 2025 Honorific + Funded Award Recipients! Meet our award winners who have contributed significantly to the #CGT field and to ASGCT. #genetherapy #celltherapy www.asgct.org/publications...
December 5, 2024 at 7:22 PM
💡 Congratulations to our 2025 Honorific + Funded Award Recipients! Meet our award winners who have contributed significantly to the #CGT field and to ASGCT. #genetherapy #celltherapy www.asgct.org/publications...
A great way to keep up with what’s happening in Cell, Gene and RNA Therapies - the latest quarterly report from ASGCT @asgct.bsky.social
www.asgct.org/global/docum...
www.asgct.org/global/docum...
www.asgct.org
November 23, 2024 at 3:58 PM
A great way to keep up with what’s happening in Cell, Gene and RNA Therapies - the latest quarterly report from ASGCT @asgct.bsky.social
www.asgct.org/global/docum...
www.asgct.org/global/docum...
At ASGCT this week, anyone else here?
May 14, 2025 at 3:10 PM
At ASGCT this week, anyone else here?
Fireside chat at ASGCT about the future of funding gene therapy
May 15, 2025 at 1:21 PM
Fireside chat at ASGCT about the future of funding gene therapy
Join @spgatucsf.bsky.social and @scopepolicy.bsky.social for this FREE hybrid Science Policy Resume Workshop led by @abankston.bsky.social, a research advocate, government relations advisor, and former AAAS/ASGCT Congressional Policy Fellow. Tue 9/29 12pm PT/3pm ET. tinyurl.com/scipol-res
September 20, 2026 at 3:00 PM
Join @spgatucsf.bsky.social and @scopepolicy.bsky.social for this FREE hybrid Science Policy Resume Workshop led by @abankston.bsky.social, a research advocate, government relations advisor, and former AAAS/ASGCT Congressional Policy Fellow. Tue 9/29 12pm PT/3pm ET. tinyurl.com/scipol-res
We're proud to share the 2026 #ASGCT Catalyst award with our collaborators at CHOP and Danaher, and even more proud to see Baby KJ thriving after receiving the first ever personalized #CRISPR therapy! Read more here: https://ow.ly/WmpP50YYtby
May 12, 2026 at 8:49 PM
We're proud to share the 2026 #ASGCT Catalyst award with our collaborators at CHOP and Danaher, and even more proud to see Baby KJ thriving after receiving the first ever personalized #CRISPR therapy! Read more here: https://ow.ly/WmpP50YYtby
Breakthrough Diabetes Gene Therapy Shows Promising Results at 2026 ASGCT Meeting#United_States#Austin#Genprex#ASGCT#diabetes_gene_therapy
Breakthrough Diabetes Gene Therapy Shows Promising Results at 2026 ASGCT Meeting
Genprex's diabetes gene therapy demonstrates significant potential for transforming Type 2 diabetes treatment at the 2026 ASGCT Annual Meeting in Austin, Texas.
third-news.com
May 14, 2026 at 12:13 PM
Breakthrough Diabetes Gene Therapy Shows Promising Results at 2026 ASGCT Meeting#United_States#Austin#Genprex#ASGCT#diabetes_gene_therapy
Join the 2026 NORD Breakthrough Summit, Oct. 25–27 in Washington, D.C.! ASGCT staff will be there to connect you with patient education resources and discuss the latest policies affecting rare disease research and individuals. Learn more ➡️ nordsummit.org
#NORDSummit #RareDisease
#NORDSummit #RareDisease
September 23, 2026 at 4:27 PM
Join the 2026 NORD Breakthrough Summit, Oct. 25–27 in Washington, D.C.! ASGCT staff will be there to connect you with patient education resources and discuss the latest policies affecting rare disease research and individuals. Learn more ➡️ nordsummit.org
#NORDSummit #RareDisease
#NORDSummit #RareDisease
ASGCT and NTSAD are launching the inaugural NTSAD-ASGCT Translational Research Fellowship Program to help advance innovative genetic medicine research for rare neurogenetic diseases.
Learn more about the fellowship, eligibility criteria and application deadlines: https://bit.ly/4hciETk
Learn more about the fellowship, eligibility criteria and application deadlines: https://bit.ly/4hciETk
September 24, 2026 at 5:00 PM
ASGCT and NTSAD are launching the inaugural NTSAD-ASGCT Translational Research Fellowship Program to help advance innovative genetic medicine research for rare neurogenetic diseases.
Learn more about the fellowship, eligibility criteria and application deadlines: https://bit.ly/4hciETk
Learn more about the fellowship, eligibility criteria and application deadlines: https://bit.ly/4hciETk
📢 Calling all ASGCT members: Apply for up to nearly $2 million in funded awards through Aug. 1! If you're a researcher growing your career, learn more about our Career Development Award + Underrepresented Populations Fellowship. bit.ly/3TgH54U #genetherapy #celltherapy #careerdevelopment
2025 Award Applications Open Through Aug. 1
This awards season, ASGCT will provide up to nearly $2 million in funded awards to members. If you@re a researcher growing your career, we invite you to take advantage of these opportunities!
bit.ly
June 6, 2025 at 6:10 PM
📢 Calling all ASGCT members: Apply for up to nearly $2 million in funded awards through Aug. 1! If you're a researcher growing your career, learn more about our Career Development Award + Underrepresented Populations Fellowship. bit.ly/3TgH54U #genetherapy #celltherapy #careerdevelopment
ASGCT is proud to lead nonprofits, academic medical centers, and patient advocacy groups in urging Congress to pass the Mikaela Naylon Give Kids a Chance Act and reauthorize the Rare Pediatric Disease Priority Review Voucher Program: https://bit.ly/4sZ2alh
Rare Pediatric Disease Priority Review Voucher (PRV) - Sign On | ASGCT
ASGCT is proud to lead nonprofits, academic medical centers, and patient advocacy groups in urging Congress to pass the Mikaela Naylon Give Kids a Chance…
www.asgct.org
January 26, 2026 at 6:57 PM
ASGCT is proud to lead nonprofits, academic medical centers, and patient advocacy groups in urging Congress to pass the Mikaela Naylon Give Kids a Chance Act and reauthorize the Rare Pediatric Disease Priority Review Voucher Program: https://bit.ly/4sZ2alh
Could gene therapy really delay the onset of Huntington's by more than a decade? With a groundbreaking approach targeting the root cause, this could redefine how we think about prevention. Curious about the details? 🧬
Latus Bio presents a gene therapy for Huntington's at ASGCT 2026 that could delay symptoms by over a decade - Sinaptica
At the annual meeting of the American Society of Gene and Cell Therapy (ASGCT 2026), held in Boston from May 11 to 15, researcher Beverly Davidson presented dat
sinapti.ca
May 15, 2026 at 5:11 PM
Could gene therapy really delay the onset of Huntington's by more than a decade? With a groundbreaking approach targeting the root cause, this could redefine how we think about prevention. Curious about the details? 🧬
"It was not a cure...."
@kiranmusunuru.bsky.social -- of Baby KJ fame -- delivered a memorable and brutally honest talk at the @asgct.bsky.social conference yesterday, on behalf of the team that won the Catalyst award.
My report for GEN:
www.genengnews.com/topics/genom...
@kiranmusunuru.bsky.social -- of Baby KJ fame -- delivered a memorable and brutally honest talk at the @asgct.bsky.social conference yesterday, on behalf of the team that won the Catalyst award.
My report for GEN:
www.genengnews.com/topics/genom...
“It Was Not a Cure”: Musunuru Cautions ASGCT on Baby KJ Promise
One of the winners of the 2026 ASGCT Catalyst Award, Kiran Musunuru, MD, PhD, delivered a sobering lecture on the legacy of the Baby KJ story and the real-world discussions with the FDA to streamline ...
www.genengnews.com
May 13, 2026 at 4:59 PM
"It was not a cure...."
@kiranmusunuru.bsky.social -- of Baby KJ fame -- delivered a memorable and brutally honest talk at the @asgct.bsky.social conference yesterday, on behalf of the team that won the Catalyst award.
My report for GEN:
www.genengnews.com/topics/genom...
@kiranmusunuru.bsky.social -- of Baby KJ fame -- delivered a memorable and brutally honest talk at the @asgct.bsky.social conference yesterday, on behalf of the team that won the Catalyst award.
My report for GEN:
www.genengnews.com/topics/genom...
*ASGCT= American Society of Gene & Cell Therapy
January 24, 2025 at 7:17 PM
*ASGCT= American Society of Gene & Cell Therapy
What does the path to leadership in cell and gene therapy look like? Scientists, Unedited host Eirini Vamva, PhD, sits down with ASGCT President Matthew Porteus, PhD, for a candid conversation about his journey, motivations, and life beyond the lab. 🎧 Listen: https://bit.ly/4uZYFea
June 25, 2026 at 6:56 PM
What does the path to leadership in cell and gene therapy look like? Scientists, Unedited host Eirini Vamva, PhD, sits down with ASGCT President Matthew Porteus, PhD, for a candid conversation about his journey, motivations, and life beyond the lab. 🎧 Listen: https://bit.ly/4uZYFea
Planning to attend the American Society of Gene & Cell Therapy Annual Meeting hosted by @asgct.bsky.social next month? Addgene will be on the ground in New Orleans for the meeting and would love to connect!
Reach out to set up a meeting with Addgene at ASGCT: www.addgene.org/cont...
#ASGCT2025
Reach out to set up a meeting with Addgene at ASGCT: www.addgene.org/cont...
#ASGCT2025
April 30, 2025 at 1:00 PM
Planning to attend the American Society of Gene & Cell Therapy Annual Meeting hosted by @asgct.bsky.social next month? Addgene will be on the ground in New Orleans for the meeting and would love to connect!
Reach out to set up a meeting with Addgene at ASGCT: www.addgene.org/cont...
#ASGCT2025
Reach out to set up a meeting with Addgene at ASGCT: www.addgene.org/cont...
#ASGCT2025
Don’t miss Amanda Hughes at #ASGCT where she’ll discuss how direct, real-time analysis of mRNA using Oxford Nanopore technology can reduce reliance on multiple assays and significantly speed up testing timelines for mRNA QC. https://bit.ly/4eqaZjl #ASGCT2026
April 27, 2026 at 4:01 PM
Don’t miss Amanda Hughes at #ASGCT where she’ll discuss how direct, real-time analysis of mRNA using Oxford Nanopore technology can reduce reliance on multiple assays and significantly speed up testing timelines for mRNA QC. https://bit.ly/4eqaZjl #ASGCT2026
Bringing a cell or gene therapy from concept to patient requires more than great science. The 2026 ASGCT Policy Summit dives into the full arc of CGT development, from pipeline funding and regulatory strategy through manufacturing, payment policy, and patient access. Join us:: asgct.org/policysummit
June 18, 2026 at 6:57 PM
Bringing a cell or gene therapy from concept to patient requires more than great science. The 2026 ASGCT Policy Summit dives into the full arc of CGT development, from pipeline funding and regulatory strategy through manufacturing, payment policy, and patient access. Join us:: asgct.org/policysummit
This afternoon on behalf of ASGCT, President-Elect Terry Flotte, MD, is attending the #WhiteHouseCGT forum! Organized by @the-white-house.bsky.social OSTP, speakers will cover challenges + opportunities in #CGTs, regulatory approaches, the patient perspective, + more!
January 8, 2025 at 4:35 PM
This afternoon on behalf of ASGCT, President-Elect Terry Flotte, MD, is attending the #WhiteHouseCGT forum! Organized by @the-white-house.bsky.social OSTP, speakers will cover challenges + opportunities in #CGTs, regulatory approaches, the patient perspective, + more!
PacBio is gearing up for #ASGCT2025 in New Orleans!
We’re excited to be part of the leading event for gene and cell therapy experts. Discover how HiFi sequencing is unlocking new possibilities in research and accelerating breakthroughs across the field.
#PacBio #ASGCT
We’re excited to be part of the leading event for gene and cell therapy experts. Discover how HiFi sequencing is unlocking new possibilities in research and accelerating breakthroughs across the field.
#PacBio #ASGCT
May 9, 2025 at 3:44 PM
PacBio is gearing up for #ASGCT2025 in New Orleans!
We’re excited to be part of the leading event for gene and cell therapy experts. Discover how HiFi sequencing is unlocking new possibilities in research and accelerating breakthroughs across the field.
#PacBio #ASGCT
We’re excited to be part of the leading event for gene and cell therapy experts. Discover how HiFi sequencing is unlocking new possibilities in research and accelerating breakthroughs across the field.
#PacBio #ASGCT
Listen to the latest episode of the Molecular Therapy podcast, Advancements in Pediatric Cancer Therapy: http://dlvr.it/TVbR90
#ChildhoodCancer #Immunotherapy
#ChildhoodCancer #Immunotherapy
Advancements in Pediatric Cancer Therapy with Nirali Shah and Timothy Cripe - ASGCT Podcast Network
Molecular Therapy Oncology has released a new special collection, Advancements in Pediatric Cancer Therapy. Listen in as guest editor Nirali Shah and Editor-in-Chief Timothy Cripe discuss articles in this special collection, which covers the history, current landscape, and future direction of pediatric cancer therapy.
Music: 'Electric Dreams' by Scott Buckley - released under CC-BY 4.0. www.scottbuckley.com.au
dlvr.it
September 22, 2026 at 12:51 PM
Listen to the latest episode of the Molecular Therapy podcast, Advancements in Pediatric Cancer Therapy: http://dlvr.it/TVbR90
#ChildhoodCancer #Immunotherapy
#ChildhoodCancer #Immunotherapy
TOMORROW: ASGCT + @fda.gov are hosting a free scientific workshop exploring immunogenicity challenges across #AAV #genetherapy treatments!
Learn perspectives from experts at @umasschan.bsky.social, @sarepta.com, and more. Register for FREE: www.asgct.org/2025aav #Immunology #RegulatoryScience #CGT
Learn perspectives from experts at @umasschan.bsky.social, @sarepta.com, and more. Register for FREE: www.asgct.org/2025aav #Immunology #RegulatoryScience #CGT
January 21, 2025 at 5:53 PM
TOMORROW: ASGCT + @fda.gov are hosting a free scientific workshop exploring immunogenicity challenges across #AAV #genetherapy treatments!
Learn perspectives from experts at @umasschan.bsky.social, @sarepta.com, and more. Register for FREE: www.asgct.org/2025aav #Immunology #RegulatoryScience #CGT
Learn perspectives from experts at @umasschan.bsky.social, @sarepta.com, and more. Register for FREE: www.asgct.org/2025aav #Immunology #RegulatoryScience #CGT