#CDKL5_Deficiency
Viralgen Partners with Elaaj Bio to Accelerate Gene Therapy for CDKL5 Deficiency Disorder#USA#Viralgen#CDKL5_Deficiency#Elaaj_Bio#San_Sebastián,_Spain
Viralgen Partners with Elaaj Bio to Accelerate Gene Therapy for CDKL5 Deficiency Disorder
Viralgen collaborates with Elaaj Bio to enhance a gene therapy program for CDKL5 deficiency disorder, a rare neurological condition affecting children.
third-news.com
May 5, 2026 at 1:23 PM
UCB Announces Positive Phase 3 Study Results for Fenfluramine in Treating CDKL5 Deficiency Disorder#United_States#Atlanta#UCB#fenfluramine#CDKL5_Deficiency
UCB Announces Positive Phase 3 Study Results for Fenfluramine in Treating CDKL5 Deficiency Disorder
UCB has revealed promising findings from the GEMZ phase 3 trial, demonstrating that fenfluramine significantly lessens seizure frequency in patients with CDKL5 deficiency disorder.
third-news.com
December 8, 2025 at 12:16 PM
UCB Unveils Positive Findings from GEMZ Phase 3 Study on Fenfluramine for Seizures#USA#Atlanta#fenfluramine#CDKL5_Deficiency#GEMZ_Study
UCB Unveils Positive Findings from GEMZ Phase 3 Study on Fenfluramine for Seizures
UCB revealed promising results from its GEMZ Phase 3 study, showing fenfluramine effectively reduces seizure frequency in patients with CDKL5 Deficiency Disorder.
third-news.com
December 8, 2025 at 6:48 AM