#LGMDR5
📌Last day at #ESGCT2026
🎤Barry Byrne will present encouraging Phase 1 results of ATA-200 for #LGMDR5.
🎤 Arnaud Valent will share updated clinical data from the GNT0004 Duchenne muscular dystrophy trial.
Advancing gene therapy from science to patients.

#GeneTherapy #DMD #ClinicalTrials #Genethon
October 30, 2026 at 7:46 AM
We are pleased to announce a new publication "Cracking the Code: Genotype–Phenotype Correlation Models in Sarcoglycanopathies" which aimed to establish accurate genotype–phenotype correlations for LGMDR3, LGMDR4, and LGMDR5 👏

bit.ly/4lGc1sL
#LGMD
Cracking the Code: Genotype–Phenotype Correlation Models in Sarcoglycanopathies
Objective Sarcoglycanopathies are among the most severe limb-girdle muscular dystrophies (LGMD), though milder presentations have been described. These diseases are primarily caused by missense vari...
bit.ly
March 20, 2026 at 9:50 AM