The 2026 #MDAconference agenda is LIVE! 🧬Join global leaders in #neuromuscular research, care & advocacy March 8-11 in Orlando FL. View tracks, speakers & sessions: www.mda.org/press-releas...

#NeuromuscularResearch #GeneticMedicine #RareDisease #ClinicalCare#RareDiseaseshtag/ClinicalCare" class="hover:underline text-blue-600 dark:text-sky-400 no-card-link">#ClinicalCarehtag/GeneticMedicine" class="hover:underline text-blue-600 dark:text-sky-400 no-card-link">#GeneticMedicineg/NeuromuscularResearch" class="hover:underline text-blue-600 dark:text-sky-400 no-card-link">#NeuromuscularResearch

Jennifer Goldstein is a specialist in Duchenne muscular dystrophy at the University of Rochester Medical Center’s Center for Health + Technology.

@mda.org #RDAatMDA #MDAConference

#MDAConference #RareDisease #RDAatMDA @mda.org

#MDAConference: Allison Moore, winner of the 2026 @mda.org Donavon Decker Community Impact in Research Award. Moore, who has Charcot-Marie-Tooth disease, is founder and CEO of the Hereditary Neuropathy Foundation.

#RareDisease #MuscularDystrophy #CharcotMarieToothDisease

Congratulations to Marwa Zafarullah, MS, PhD, for presenting her amazing research in Dr. John Day's Lab at the MDA Conference 2026 in Orlando (Mar 8–11). The meeting drew 2,366 attendees from 44 countries and highlighted advances in neuromuscular science and care. #MDAConference #Neuromuscular

Presenting new data @MDAorg Clinical & Scientific Conference highlighting potential of genetic medicine using targeted, ultrasound-mediated delivery in treating DMD. Learn more: sonothera.com/press-releases #geneticmedicine #ultrasound #ultrasoundmediated #SonoThera #MDAconference #MuscularDystrophy

#MDAConference: Craig McDonald, MD, Director of the Neuromuscular Disease Clinic at @ucdavishealth.bsky.social, speaking about @sarepta.com's gene therapy delandistrogene moxeparvovec-rokl (#Elevidys) for #Duchenne at the @mda.org's 2026 Clinical & Scientific Conference in Orlando, FL.

The Medlive team recently shared research at the #MDAconference with our poster on advancing clinician education in #BeckerMuscularDystrophy. Developed with @nordrare.bsky.social & MDA, this #CME initiative explores improving clinician awareness & preparedness for emerging therapies.

bit.ly/47u8LuJ

#MDAConference: "Really the relative risk versus benefits in older DMD patients with preexisting cardiomyopathy or history of heart failure is currently unknown."
-Beth Kaufman, MD, Director, Pediatric Cardiomyopathy Program at Stanford Medicine Children's Health

#RDAatMDA @mda.org

In an oral presentation at the MDA Clinical & Scientific Conference next week, we will present preclinical data for our lead, rationally designed, RNA-targeted small molecule drug program for treatment of myotonic dystrophy type 1 (DM1). #MDAconference #ExpeditionRNA
arrakistx.com/press-releas...

🧬 Two phase 3 trials are underway to evaluate salanersen in presymptomatic newborns with spinal muscular atrophy.

The STELLAR-1 and STELLAR-2 studies will assess outcomes with salanersen alone or following gene therapy.

Presented at the 2026 #MDAconference
#SMA #Neurology #GeneTherapy #RareDisease

#MDAConference: We spoke with Chris Lewis, son of world-famous comedian Jerry Lewis, who through his annual telethons helped raise $2.5 billion for @mda.org

#RDAatMDA

#MDAConference: Susan Apkon, MD, pediatric neurologist at @childrenscolo.bsky.social speaking March 9 about Duchenne muscular dystrophy at the 2026 @mda.org Clinical & Scientific Conference in Orlando, FL.

#RareDisease #MuscularDystrophy #DuchenneMuscularDystrophy

🚨 Registration is OPEN! 🚨
Join us March 8–11, 2026 in Orlando for the #MDAConference, the leading global event for neuromuscular care & research. 🌍🧬

🔗 Register now: www.mdaconference.org

#MDA #MuscularDystrophy #neuromuscular

#MDAConference: "It's important that we're empowering our patients through education and self-management strategies." -Constance de Monts, PT, DPT Neuromuscular Clinical Research Manager/Evaluator at @stanfordmedicine.bsky.social.

@mda.org #RDAatMDA

#MDAConference: Barry Byrne, MD, PhD, Gene therapy expert and Board Member of the @mda.org, speaking at the MDA’s 2026 Clinical & Scientific Conference in Orlando, FL.

#RareDisease #MuscularDystrophy #Duchenne

The winner of the first ever @mda.org Legacy Award for Community Impact in Research goes to Donovan Decker, a South Dakota patient and advocate with limb-girdle muscular dystrophy.

#MDAConference #RDAatMDA

#MDAConference: Katherine Mathews, MD, director of the Iowa Neuromuscular Program wins the 2025 MDA Legacy Award for her contributions to the understanding and treatment of #GeneticDisorders affecting the neuromuscular system.

@mda.org #RDAatMDA #RareDisease

#mdaconference: “Medicine as a business is winning out right now over medicine as a profession—not just doctors but all the clinicians involved in multidisciplinary care … I hope I’m wrong.”
- Former FDA Commissioner Robert M. Califf

#RDAatMDA @mda.org

Today at the Muscular Dystrophy Association Clinical & Scientific Conference, Domi Stickens, PhD, CSO, presents a poster highlighting our RNA-targeted small-molecule therapeutics and first oral therapy in development for myotonic dystrophy type 1 (DM1).
#MDAconference #ArrakeensInAction

#MDAConference: Edward Neilan, Chief Medical and Scientific Officer at @nordrare.bsky.social, speaking at the @mda.org's 2026 Clinical & Scientific Conference in Orlando, FL.

#RareDisease #MuscularDystrophy #AI #MedTech

#MDAConference: Sharon Hesterlee, MD, president and CEO of the Muscular Dystrophy Association, opening the @mda.org’s 2026 Clinical & Scientific Conference in Orlando, FL.

#RareDisease #MuscularDystrophy #MedSky

Catch up with Hugh Bartlett at the #MDAconference from March 8-11 in Orlando, FL! Don’t miss the opportunity to explore the latest research advancements and clinical progress in #neuromuscular diseases.
To connect with Hugh: hbartlett@rarelifesolutions.com
#MuscularDystrophy #MDA #RareLifeSolutions

🧬 Had a fantastic time at the #MDA Conference in Orlando! I shared some of our work on titin (TTN). Great discussions and new ideas sparked with colleagues working on #titin related myopathies. Excited for what comes next! 💪 #MDAConference @myofinlab.bsky.social @folkhalsanresearch.bsky.social

#MDAConference: Łukasz J Sznajder, PhD, an assistant professor at the @unlv.edu, and winner of the 2026 @mda.org Research Momentum Award

Image & quote taken by Senior Correspondent, Larry Luxner.

#RareDisease #MuscularDystrophy