@novartis.bsky.social #genetherapy #spinalmuscularatrophy #SMAtreatment #OAV101IT #onasemnogeneabeparvovec #typeIISMApatients #intrathecalformaulation #STEERstudy #genetransfertherapy #typeIIspinalmuscularatrophy #SMAawareness #Zolgensma #IVformulation #Neurology
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Novartis gene therapy set to enhance SMA treatment - PharmaTimes
OAV101 IT expands potential for type II SMA patients
pharmatimes.com
January 8, 2025 at 10:12 AM