#genetherapy
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mkybooksdigital.bsky.social
What if scientists could rewrite the code of human life? 🧬
#crispr #geneticengineering #genetherapy #biotechnology #bioethics #genomeediting #sciencebooks
Book link: a.co/d/0h9yA1lG
November 4, 2026 at 2:45 PM
haythamm.bsky.social
#GeneTherapy showing yet more promise...
covid19disease.bsky.social SARS‑CoV‑2 (COVID-19) @covid19disease.bsky.social · 5h
🚨 BREAKTHROUGH: Doctors in Houston Report Complete Disappearance of Aggressive Liver Cancer in a 3-Year-Old Using a Personalized Immunotherapy Made From the Child’s Own Cells No Cancer Detected One Year Late
November 4, 2026 at 2:26 PM
chemcenterbio.bsky.social
Can 84.6% Protein Restoration Reverse Autism Social Deficits? 🧬

Source: Gene Therapy Journal (2026), bioRxiv (2026)

#autismresearch #neuroscience #genetherapy #neuroplasticity
November 4, 2026 at 5:57 PM
chemcenterbio.bsky.social
🧠 Can 4 days of eFT508 lock in 9 weeks of relief?

Source: Nature Neuroscience, Neuron, Cell Reports

​#autismresearch #neuroscience #peptides #genetherapy #neurodevelopment #biotech #brainhealth #nootropics #sciencefacts #molecularbiology
November 4, 2026 at 4:06 AM
realfeedapp.com
The AI agent selected the drug, identified brain coordinates, and injected 250 nanolitres while a vet monitored irreversible steps.

#AIAgent #BrainSurgery #GeneTherapy
AI agent performed brain surgery on a mouse
Source: HackerNews front
realfeedapp.com
November 3, 2026 at 8:40 AM
haemnet.bsky.social
We're pleased to share news of the publication of Simon Fletcher's lived experience model for #psychosocial support in the age of #haemophilia #genetherapy as a Letter to the Editor in Haemophilia.

#HemeSky #MedSky
November 3, 2026 at 8:30 AM
straits2026.bsky.social
Cell and Gene Therapy is transforming modern medicine through innovative treatments and advanced genetic technologies. Discover key industry trends and growth opportunities.

#CellTherapy #GeneTherapy #Healthcare
Cell and Gene Therapy Market
November 3, 2026 at 11:59 AM
drtimos.bsky.social
🚀 Big buzz at #ASGCT25: #GeneEditing & #CRISPR headlines, 20% data-driven talk, 85% positive vibes on breakthrough therapies for #DMD & #rarediseases!🧬 Download our full #socialmedia report! http://dlvr.it/TW6zCB #GeneTherapy #SocialListening #LucidQuest
@ASGCTherapy @ESGCT
October 30, 2026 at 4:00 PM
chemcenterbio.bsky.social
Did A New Gene Blocker Just Restore Speech Pathways In 2026? 🧬🧠⚡ Nex-Gen Autism Protocol?

Source: Roh et al., Nature Communications (SLC6A20 ASO Synaptic Rescue Study, 2026)

#slc6a20 #neuroscience #brainhealth #geneediting #genetherapy #biotechnology #neurodevelopment #synapse #preclinical
November 3, 2026 at 4:08 PM
realfeedapp.com
The agency issued final guidance requiring manufacturers to implement a potency assurance strategy across the entire lifecycle of cell and gene therapy products to ensure batch consistency before patient delivery.

#CellTherapy #GeneTherapy #FDA
FDA issues new rules for cell therapy potency testing
Source: FDA
realfeedapp.com
November 3, 2026 at 7:20 AM
wavedeva.bsky.social
#SickleCellDisease #GeneTherapy
October 26, 2026 at 7:01 PM
markfortner.bsky.social
A Claude model autonomously chose a gene therapy and operated on a mouse brain with no human decision-making | #AI #GeneTherapy
A Claude model autonomously chose a gene therapy and operated on a mouse brain with no human decision-making
An AI agent performed brain surgery on an epileptic mouse, picking the drug, the brain target, and the injection coordinates on its own. According to lead researcher Ocana-Santero, it's the first time...
the-decoder.com
November 1, 2026 at 4:13 PM
pharmaj.bsky.social
The Medicines and Healthcare products Regulatory Agency has approved a gene-editing treatment for severe sickle-cell disease and transfusion-dependent β-thalassemia for patients aged five years and older

#ukpharmacy #genetherapy

buff.ly/fhSRz95
MHRA extends approval for gene-editing therapy to patients aged five years and over
The Medicines and Healthcare products Regulatory Agency (MHRA) has approved a gene-editing treatment for severe sickle-cell disease and transfusion-dependent β-thalassemia for patients aged five…
buff.ly
November 2, 2026 at 3:15 PM
wimi-bio-tech.bsky.social
Chinese researchers engineered an ultra-compact Cas12m variant (denCas12m) to create smCRISPRa, enabling single-AAV multiplex gene activation of up to 6 genes and therapeutic rescue in mouse models of Dravet syndrome and DMD. 🧬🤖 #CRISPRa #AAV #GeneTherapy #Cas12m #NatureBiotech #DMD #DravetSyndrome
November 2, 2026 at 6:36 AM
pharmaphorum.bsky.social
An #invivo #genetherapy for alpha-1 antitrypsin deficiency (#AATD) developed by Chinese biotech #YolTech has successfully treated a patient with the PiZZ form of the rare inherited disorder.

pharmaphorum.com/news/case-st...
Case study backs YolTech's AATD gene therapy
A gene therapy for alpha-1 antitrypsin deficiency developed by China's YolTech has successfully treated a patient with a severe form of the disease.
pharmaphorum.com
November 3, 2026 at 2:10 PM
pharmaphorum.bsky.social
The #FDA is due to deliver a decision on #uniQure's #genetherapy for neurodegenerative disorder #Huntingtons by 1st May next year, after granting a #priorityreview for the candidate.

pharmaphorum.com/news/uniqure...
uniQure set for May FDA verdict on Huntington's gene therapy
The FDA has started its review of uniQure's gene therapy for neurodegenerative disorder Huntington's, but will require an advisory committee meeting.
pharmaphorum.com
November 3, 2026 at 12:15 PM
aidailypost.com
Claude’s AI just picked a gene‑therapy target and ran a mouse brain surgery—no human call‑offs. What does this mean for biotech and AI ethics? Dive into the details. #ClaudeAI #GeneTherapy #NeuroAI

🔗 aidailypost.com/news/claude-...
October 30, 2026 at 8:25 PM
drtimos.bsky.social
🚀 Big buzz at #ASGCT25: #GeneEditing & #CRISPR headlines, 20% data-driven talk, 85% positive vibes on breakthrough therapies for #DMD & #rarediseases!🧬 Download our full #socialmedia report! http://dlvr.it/TW6zCB #GeneTherapy #SocialListening #LucidQuest
@ASGCTherapy @ESGCT
October 30, 2026 at 4:00 PM
aidailypost.com
Claude’s AI just picked a gene‑therapy target and ran a mouse brain surgery—no human call‑offs. What does this mean for biotech and AI ethics? Dive into the details. #ClaudeAI #GeneTherapy #NeuroAI

🔗 aidailypost.com/news/claude-...
October 30, 2026 at 8:25 PM
pharmalot.bsky.social
Pharmalot.. Pharmalittle.. Good Morning: We’re reading about a generic HIV prevention shot, Lonza buying U.S. facilities and more news.. statnews.com/pharmalot/20... #pharma #HIV #mpox #genetherapy #Uniqure #AstraZeneca #India #AbbVie #Teva #Lonza #generics #medicine
Pharmalittle: We're reading about a generic HIV prevention shot, Lonza buying U.S. facilities, and more
The FDA gave tentative approval to Dr. Reddy’s Laboratories to make a generic version of a groundbreaking HIV prevention medicine
statnews.com
November 3, 2026 at 3:14 PM
fionarobinsonphd.bsky.social
In this week's NBDF Wednesday Webinar our expert panel will discuss some of the eligibility, access, insurance, advocacy, and psychosocial challenges of #GeneTherapy for #hemophilia
Bring your questions for the live Q&A!
2PM ET, Nov 4
Pre-register (FREE!): bleeding.org/events
Upcoming Events for the Bleeding Disorders Community | NBDF
Discover in-person and virtual events to connect with the bleeding disorders community. Stay informed about upcoming gatherings, workshops, and conferences.
bleeding.org
November 2, 2026 at 8:31 PM
genethonfr.bsky.social
📌Last day at #ESGCT2026
🎤Barry Byrne will present encouraging Phase 1 results of ATA-200 for #LGMDR5.
🎤 Arnaud Valent will share updated clinical data from the GNT0004 Duchenne muscular dystrophy trial.
Advancing gene therapy from science to patients.

#GeneTherapy #DMD #ClinicalTrials #Genethon
October 30, 2026 at 7:46 AM
interestingpatents.bsky.social
A patent application from the University of Pennsylvania #UPenn, #US20260327656A1, describes an AAV-based gene-delivery composition designed to provide functional survival motor neuron (SMN) protein for spinal muscular atrophy (SMA). #GeneTherapy
Fig. 01 from patent document #US20260327656 Fig. 04 from patent document #US20260327656 Fig. 36 from patent document #US20260327656
October 30, 2026 at 3:35 PM
neurologylive.bsky.social
🧬 🆕 interim BB-301 data in OPMD: All 9 patients met formal response criteria in a phase 1b/2a trial, with no serious AEs reported

🔎 Read more: www.neurologylive.com/view/benitec...
#OPMD #GeneTherapy #Clinical #ClinicalTrial #Neurology
Benitec Reports Positive Interim Results for BB-301 in Oculopharyngeal Muscular Dsytrophy | NeurologyLive - Clinical Neurology News and Neurology Expert Insights
Interim phase 1b/2a data showed all patients treated with high- or low-dose BB-301 for oculopharyngeal muscular dystrophy met formal response criteria.
www.neurologylive.com
November 3, 2026 at 4:45 PM
qkine.bsky.social
We're excited to be heading to Boston for @Advanced Therapies USA 2027!

More about the event > zurl.co/fIqFj

We looking forward to talking about our range of animal-free Cell Therapy Grade proteins > zurl.co/taYQo

#animalfree #celltherapy #genetherapy
October 27, 2026 at 8:18 AM