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hdreachgameoverhd.bsky.social
Join the Fight to Bring Hope to HD Families: Urge the FDA to Uphold Accelerated Approval!

www.change.org/p/bring-hope...

#hdreachgameoverhd #huntingtonsdisease #fyp #raredisease #amt130 #fda #advocacy #petition
November 25, 2025 at 10:09 PM
azat.tv
Gene therapy developer uniQure announced plans to submit a Biologics License Application for its Huntington’s disease treatment, AMT-130, following positive feedback from the FDA.

https://azat.tv/en/uniqure-amt130-fda-submission/
uniQure to Submit Huntington’s Gene Therapy for FDA Approval
June 17, 2026 at 7:48 PM
profwild.bsky.social
And Uniqure’s AMT130 gene therapy safe & well tolerated at 24mo (low dose), 12mo (high). Claims of efficacy signal less clear but NFL below baseline is definitely encouraging & should be helped by short steroid treatment of future cases

https://www.uniqure.com/investors-media/press-releases
June 21, 2023 at 12:30 PM
cronicadelhenares.bsky.social
CIENCIA. El AMT-130 se posiciona como el "santo grial" contra la enfermedad de Huntington. Según expertos, esta terapia génica pionera ofrece los datos más sólidos vistos hasta hoy. Lee más aquí: www.cronicadelhenares.com/2025/12/salu... #AMT130 #Neurología #Huntington #Salud #TerapiaGénica
SALUD. AMT-130: ¿El "Santo Grial" contra la Enfermedad de Huntington?
salud, fármacos, AMT-130, Enfermedad de Huntington, neurociencia, terapias génicas
www.cronicadelhenares.com
December 8, 2025 at 7:07 PM
rarediseaseadvisor.bsky.social
AMT-130, an investigational #GeneTherapy for #HuntingtonDisease (HD), will likely require a large controlled trial before it can be considered for approval, uniQure announced.

Read more: https://bit.ly/4sfOrFo

#RareDisease #AMT130 #ClinicalTrial
HD Gene Therapy AMT-130 Faces Requirement for Large Controlled Trial Before FDA Approval
AMT-130, an investigational gene therapy for HD, will likely require a large controlled trial before the FDA will consider it for approval.
www.rarediseaseadvisor.com
March 4, 2026 at 5:15 PM
kstrategyand.bsky.social
www.linkedin.com/pulse/fda-ad...

FDA Advances uniQure’s Groundbreaking Gene Therapy for Huntington’s

kstrategyand.com

#uniQure #AMT130 #HuntingtonsDisease #GeneTherapy #HuntingtonsResearch #Humanteconomy #Humantec #KStrategyand
FDA Advances uniQure’s Groundbreaking Gene Therapy for Huntington’s
uniQure has achieved a critical milestone in the pursuit of an innovative therapy for Huntington’s disease, securing FDA alignment on key aspects of the Accelerated Approval pathway for AMT-130. This ...
www.linkedin.com
December 20, 2024 at 10:50 AM