#GeneEditingTherapy
LightNews LightNews
rarediseaseadvisor.bsky.social
The @fda.gov has approved the Investigational New Drug (#IND) application for YOLT-202, an in vivo gene-editing therapy for alpha-1 antitrypsin deficiency (#AATD), according to a recent press release.

Read more: https://bit.ly/4draiFV

#RareDisease #YOLT202 #GeneEditingTherapy #Alpha1
FDA Gives Clearance to In Vivo Gene-Editing Therapy for AATD
The FDA has approved the Investigational New Drug application for YOLT-202, an in vivo gene-editing therapy for AATD.
bit.ly
April 3, 2026 at 3:20 PM
4040rec.bsky.social
#haematology #Sicklecelldisease #sicklecellgenetherapy #genetherapy #geneeditingtherapy #Casgevy #Exacel @vertexpharma.bsky.social #NHS #haemoglobin #clinicaltrials #functionalcure @AmandaPritchard #geneeditingtool #Crispr #editedstemcells #NHSEngland #clinicaltrials
www.bbc.co.uk/news/article...
NHS to offer 'groundbreaking' sickle cell gene therapy
The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts say.
www.bbc.co.uk
February 3, 2025 at 1:36 PM
indiaabroad.bsky.social
#TIME names five #IndianAmerican health leaders in #TIME100Health for shaping #globalhealthcare in #AIEnabledCare, personalized #GeneEditingTherapy, #OpioidSurveillance and harm reduction, #CancerScreeningResearch, and #OncologyInnovation.

https://ow.ly/6UPA50YezQX
February 12, 2026 at 9:15 PM
bionewscentral.com
Landmark study showcases the power of personalized #CRISPR #GeneEditingTherapy to treat a patient with rare #MetabolicDisease.
#GeneEditing #PersonalizedMedicine
World's first patient treated with personalized CRISPR gene editing therapy – BioNews Central
Landmark study showcases the power of personalized CRISPR gene editing therapy to treat a patient with rare metabolic disease. ...
sbee.link
May 23, 2025 at 11:54 PM