Happy MPS Awareness Day 💜
Today was my weekly Vimizim infusion for Morquio syndrome.
Forgive the rather distressing-looking image, it’s nowhere near as traumatic as it looks.
Living with MPS IV isn’t easy, but awareness, research and support matter.
🔗 cutt.ly/StVSIey9
#MPSAwarenessDay #Morquioq
Today was my weekly Vimizim infusion for Morquio syndrome.
Forgive the rather distressing-looking image, it’s nowhere near as traumatic as it looks.
Living with MPS IV isn’t easy, but awareness, research and support matter.
🔗 cutt.ly/StVSIey9
#MPSAwarenessDay #Morquioq
May 15, 2026 at 3:01 PM
Happy MPS Awareness Day 💜
Today was my weekly Vimizim infusion for Morquio syndrome.
Forgive the rather distressing-looking image, it’s nowhere near as traumatic as it looks.
Living with MPS IV isn’t easy, but awareness, research and support matter.
🔗 cutt.ly/StVSIey9
#MPSAwarenessDay #Morquioq
Today was my weekly Vimizim infusion for Morquio syndrome.
Forgive the rather distressing-looking image, it’s nowhere near as traumatic as it looks.
Living with MPS IV isn’t easy, but awareness, research and support matter.
🔗 cutt.ly/StVSIey9
#MPSAwarenessDay #Morquioq
Today is #MPSAwarenessDay.
#Hurlersyndrome is a severe form of MPS and is associated with significant disease burden, impacting quality of life and life expectancy.
We recently announced AX-0422, a potential #RNAEditing therapy in development for Hurler syndrome.
#ShineforMPS
#Hurlersyndrome is a severe form of MPS and is associated with significant disease burden, impacting quality of life and life expectancy.
We recently announced AX-0422, a potential #RNAEditing therapy in development for Hurler syndrome.
#ShineforMPS
May 15, 2026 at 8:44 AM
Today is #MPSAwarenessDay.
#Hurlersyndrome is a severe form of MPS and is associated with significant disease burden, impacting quality of life and life expectancy.
We recently announced AX-0422, a potential #RNAEditing therapy in development for Hurler syndrome.
#ShineforMPS
#Hurlersyndrome is a severe form of MPS and is associated with significant disease burden, impacting quality of life and life expectancy.
We recently announced AX-0422, a potential #RNAEditing therapy in development for Hurler syndrome.
#ShineforMPS
On International #MPSAwarenessDay, we stand with individuals affected by mucopolysaccharidoses (MPS) and mucolipidoses (ML), rare lysosomal storage disorders associated with progressive multisystem disease. Awareness drives earlier diagnosis, research, and action.
#MLAwareness #ForUsItsPersonal
#MLAwareness #ForUsItsPersonal
May 15, 2026 at 2:06 PM
On International #MPSAwarenessDay, we stand with individuals affected by mucopolysaccharidoses (MPS) and mucolipidoses (ML), rare lysosomal storage disorders associated with progressive multisystem disease. Awareness drives earlier diagnosis, research, and action.
#MLAwareness #ForUsItsPersonal
#MLAwareness #ForUsItsPersonal
Today, May 15, we proudly observe #MPSAwarenessDay and stand in solidarity with the #MPS community. We thank our patients who participated in the prenatal ERT #PEARLTrial. Their courage and their contributions are humbling. Meet one of these inspiring families: bit.ly/3OgxCZD #MPSAwarenessDay2025
Fetal therapy offers hope for unborn patients suffering from the rare genetic disease Hunter Syndrome
Some parents-to-be have to face the terrifying news that their unborn child has been diagnosed with a life-threatening genetic disorder.
bit.ly
May 15, 2025 at 12:27 PM
Today, May 15, we proudly observe #MPSAwarenessDay and stand in solidarity with the #MPS community. We thank our patients who participated in the prenatal ERT #PEARLTrial. Their courage and their contributions are humbling. Meet one of these inspiring families: bit.ly/3OgxCZD #MPSAwarenessDay2025
