#Genetherapy
Breaking science news - Huntington's disease, which is a brutal and destructive genetic condition, has just been successfully treated for the first time, and the results are incredible.

youtube.com/shorts/lECCw...
Incredible Huntington's disease breakthrough announced #sciencenews #medicalscience #genetherapy
YouTube video by Zion Lights
youtube.com
September 24, 2025 at 3:06 PM
A breakthrough gene therapy is slowing Huntington’s disease — and NASA’s James Webb has spotted strange “dark beads” floating in Saturn’s atmosphere. Two discoveries, one Science Sunday.

#ScienceSunday #HuntingtonsDisease #GeneTherapy #Saturn #JWST #SpaceNews #BreakingScience
September 28, 2025 at 9:50 AM
At the White House Cell and Gene Therapy Forum with my former @mskcancercenter.bsky.social colleague Kamal Menghrajani #cancermoonshot #whitehousecgt #genetherapy #CARTcells
January 8, 2025 at 6:42 PM
A 31-year-old Sligo man who was functionally blind has got his sight back, after being treated with a new gene therapy at the Mater University Hospital in Dublin.
Functionally blind man gets sight back after gene therapy
A 31-year-old Sligo man who was functionally blind has got his sight back, after being treated with a new gene therapy at the Mater University Hospital in Dublin.
www.rte.ie
February 18, 2025 at 3:12 PM
On my way to @ash-hematology.bsky.social #ASH24 & sharing this starterpack for HCT, #CARTcells & #genetherapy - > 100 members DM/comment if I missed someone #bmtsm #mmsm #leusm #lymsm #sicklecell #mpnsm #medsky

go.bsky.app/7xxh8WW
December 5, 2024 at 12:32 PM
A wonderful response to this article yesterday folks. Thanks for liking and reposting! It was so great to have some good news...

#SickleCell
#GeneTherapy
A major breakthrough in gene therapy for the treatment of sickle cell disease
CRISPR/Cas9, a powerful gene-editing technology has been successfully used to treat sickle cell disease, a painful life-threatening inherited blood disorder
bylines.scot
February 27, 2025 at 7:49 AM
Happy to welcome #ASTCT to @bsky.app Follow @astct.bsky.social as we prepare for #Tandem25 in Honolulu #bmtsm #CARTcells #genetherapy
December 10, 2024 at 10:40 PM
Great starter pack for those of us In hematopoietic stem cell and T cell therapies. 💙🩵 #celltherapy #immunotherapy #genetherapy #CART
go.bsky.app/7xxh8WW
November 23, 2024 at 12:11 PM
Happy new year everyone and I 've an exciting announcement to make: @naturecellbiology.bsky.social is now open to considering #preclinical studies & #ClinicalTrials, including #CellTherapy or #genetherapy, among others. Feel free to contact the handling editor for more info (yes, that 'd be me!)
January 1, 2025 at 7:47 PM
Gene therapy is a promising method for treating cancer #genetherapy #genetics #cancertreatment ... Continue to: www.facebook.com/reel/1058042...
Gene therapy is a promising method for treating cancer #genetherapy #genetics #cancertreatment
Gene therapy is a promising method for treating cancer #genetherapy #genetics #cancertreatment
www.facebook.com
August 9, 2026 at 10:11 PM
The Human Genome Project didn’t end genomics—it opened the door.
Its sequence helped fuel #precisionmedicine, #cancergenomics, #genetherapy and #genomeediting.
And it revealed a deeper question:
🧬 How is the genome regulated? Enter the world of #Epigenetics.
#HumanGenomeProject #HGP #Genomics
October 1, 2026 at 4:05 AM
👀: #Genetherapy #Zolgensma has helped babies born with #SMA grow up to run and play. It’s $2m price is absorbed by all Americans in the form of rising #healthinsurance premiums & #taxes for programs like #Medicaid ($309m spent on just 208 claims in 4 yrs.)

📰: Robin Fields
🎨: @owengent.bsky.social
February 21, 2025 at 5:29 PM
🧬 CRISPR just levelled up

A new tool, evoCAST, can insert entire genes into human DNA, with no cutting required.

Hopefully this is one step closer to safe, scalable gene therapies.

🔗 doi.org/10.1038/d415...

#SciComm #CRISPR #GeneTherapy 🧪
Powerful CRISPR system inserts whole gene into human DNA
‘Directed’ evolution in the laboratory creates an editing tool that outperforms classic CRISPR systems.
doi.org
May 21, 2025 at 4:53 AM
🧪Current Base Editing clinical trials, from David Liu
#geneediting #genetherapy
November 20, 2024 at 2:37 PM
KNOW NUT NOVEMBER-19:

it's working.

#nnn #nonutnovember
November 19, 2025 at 10:42 AM
The Cellicon Valley wallpaper has a home here. #cellthetherapy #genetherapy #innovation #Philly
November 30, 2024 at 1:53 PM
All mic’d up and ready for my @crick.ac.uk crash course on #GeneTherapy!
July 2, 2025 at 8:49 AM
Previously on Bylines Scotland ... a bit of good news!

#SickleCell
#GeneTherapy
A major breakthrough in gene therapy for the treatment of sickle cell disease
CRISPR/Cas9, a powerful gene-editing technology has been successfully used to treat sickle cell disease, a painful life-threatening inherited blood disorder
bylines.scot
March 11, 2025 at 2:45 PM
GeneH is bringing gene therapy research into higher education at the University of Coimbra.
Explore its portfolio for Master’s and PhD programmes, from teaching modules to a proposed doctoral pathway.

www.uc.pt/en/geneh/new...

#GeneH #GeneTherapy
@kemijski.bsky.social @ctgct.bsky.social
September 28, 2026 at 8:33 AM
A landmark gene therapy study! Out today with NEJM

AAV mediated gene replacement of LAMP2 in boys with Danon disease Phase 1 trial demonstrates a reasonable safety profile

www.nejm.org/doi/pdf/10.1...

This is a big deal

#cardiosky #medsky #genetherapy #Dana at #AHA24 @ahascience.bsky.social
November 18, 2024 at 8:54 PM
A single treatment that could end HAE attacks for good: https://bit.ly/3FHecMk

Gene therapy research is bringing us closer to that reality.

#HAE #HereditaryAngioedema #GeneTherapy #CRISPR #RareDisease #AngioedemaNews #Bionews
September 28, 2026 at 6:46 PM