#geneTherapy
Breaking science news - Huntington's disease, which is a brutal and destructive genetic condition, has just been successfully treated for the first time, and the results are incredible.

youtube.com/shorts/lECCw...
Incredible Huntington's disease breakthrough announced #sciencenews #medicalscience #genetherapy
YouTube video by Zion Lights
youtube.com
September 24, 2025 at 3:06 PM
A breakthrough gene therapy is slowing Huntington’s disease — and NASA’s James Webb has spotted strange “dark beads” floating in Saturn’s atmosphere. Two discoveries, one Science Sunday.

#ScienceSunday #HuntingtonsDisease #GeneTherapy #Saturn #JWST #SpaceNews #BreakingScience
September 28, 2025 at 9:50 AM
At the White House Cell and Gene Therapy Forum with my former @mskcancercenter.bsky.social colleague Kamal Menghrajani #cancermoonshot #whitehousecgt #genetherapy #CARTcells
January 8, 2025 at 6:42 PM
A 31-year-old Sligo man who was functionally blind has got his sight back, after being treated with a new gene therapy at the Mater University Hospital in Dublin.
Functionally blind man gets sight back after gene therapy
A 31-year-old Sligo man who was functionally blind has got his sight back, after being treated with a new gene therapy at the Mater University Hospital in Dublin.
www.rte.ie
February 18, 2025 at 3:12 PM
On my way to @ash-hematology.bsky.social #ASH24 & sharing this starterpack for HCT, #CARTcells & #genetherapy - > 100 members DM/comment if I missed someone #bmtsm #mmsm #leusm #lymsm #sicklecell #mpnsm #medsky

go.bsky.app/7xxh8WW
December 5, 2024 at 12:32 PM
A wonderful response to this article yesterday folks. Thanks for liking and reposting! It was so great to have some good news...

#SickleCell
#GeneTherapy
A major breakthrough in gene therapy for the treatment of sickle cell disease
CRISPR/Cas9, a powerful gene-editing technology has been successfully used to treat sickle cell disease, a painful life-threatening inherited blood disorder
bylines.scot
February 27, 2025 at 7:49 AM
Happy to welcome #ASTCT to @bsky.app Follow @astct.bsky.social as we prepare for #Tandem25 in Honolulu #bmtsm #CARTcells #genetherapy
December 10, 2024 at 10:40 PM
Great starter pack for those of us In hematopoietic stem cell and T cell therapies. 💙🩵 #celltherapy #immunotherapy #genetherapy #CART
go.bsky.app/7xxh8WW
November 23, 2024 at 12:11 PM
Happy new year everyone and I 've an exciting announcement to make: @naturecellbiology.bsky.social is now open to considering #preclinical studies & #ClinicalTrials, including #CellTherapy or #genetherapy, among others. Feel free to contact the handling editor for more info (yes, that 'd be me!)
January 1, 2025 at 7:47 PM
Gene therapy is a promising method for treating cancer #genetherapy #genetics #cancertreatment ... Continue to: www.facebook.com/reel/1058042...
Gene therapy is a promising method for treating cancer #genetherapy #genetics #cancertreatment
Gene therapy is a promising method for treating cancer #genetherapy #genetics #cancertreatment
www.facebook.com
August 9, 2026 at 10:11 PM
The Human Genome Project didn’t end genomics—it opened the door.
Its sequence helped fuel #precisionmedicine, #cancergenomics, #genetherapy and #genomeediting.
And it revealed a deeper question:
🧬 How is the genome regulated? Enter the world of #Epigenetics.
#HumanGenomeProject #HGP #Genomics
October 1, 2026 at 4:05 AM
👀: #Genetherapy #Zolgensma has helped babies born with #SMA grow up to run and play. It’s $2m price is absorbed by all Americans in the form of rising #healthinsurance premiums & #taxes for programs like #Medicaid ($309m spent on just 208 claims in 4 yrs.)

📰: Robin Fields
🎨: @owengent.bsky.social
February 21, 2025 at 5:29 PM
🧬 CRISPR just levelled up

A new tool, evoCAST, can insert entire genes into human DNA, with no cutting required.

Hopefully this is one step closer to safe, scalable gene therapies.

🔗 doi.org/10.1038/d415...

#SciComm #CRISPR #GeneTherapy 🧪
Powerful CRISPR system inserts whole gene into human DNA
‘Directed’ evolution in the laboratory creates an editing tool that outperforms classic CRISPR systems.
doi.org
May 21, 2025 at 4:53 AM
🧪Current Base Editing clinical trials, from David Liu
#geneediting #genetherapy
November 20, 2024 at 2:37 PM
KNOW NUT NOVEMBER-19:

it's working.

#nnn #nonutnovember
November 19, 2025 at 10:42 AM
The Cellicon Valley wallpaper has a home here. #cellthetherapy #genetherapy #innovation #Philly
November 30, 2024 at 1:53 PM
All mic’d up and ready for my @crick.ac.uk crash course on #GeneTherapy!
July 2, 2025 at 8:49 AM
Previously on Bylines Scotland ... a bit of good news!

#SickleCell
#GeneTherapy
A major breakthrough in gene therapy for the treatment of sickle cell disease
CRISPR/Cas9, a powerful gene-editing technology has been successfully used to treat sickle cell disease, a painful life-threatening inherited blood disorder
bylines.scot
March 11, 2025 at 2:45 PM
A landmark gene therapy study! Out today with NEJM

AAV mediated gene replacement of LAMP2 in boys with Danon disease Phase 1 trial demonstrates a reasonable safety profile

www.nejm.org/doi/pdf/10.1...

This is a big deal

#cardiosky #medsky #genetherapy #Dana at #AHA24 @ahascience.bsky.social
November 18, 2024 at 8:54 PM
Excited to be in DC to represent @astct.bsky.social at the #WhiteHouse Cell and Gene Therapy Forum. Let’s continue to push innovation & access in this field to bring novel therapies to our patients. #genetherapy #CARTcells
January 8, 2025 at 3:03 AM
Imagine finding out the notorious dictator of one of the last open major dictatorships in the sol system has an onlyfans where he dresses in frilly clothes and shakes his big meaty genetherapy perfected pecs around like an anime girl

This is Yan Vansike, Banner-Prince of Titan in a nutshell
February 16, 2026 at 5:27 AM